Liver-Directed Adeno-Associated Virus–Mediated Gene Therapy for Mucopolysaccharidosis Type VI
Nicola Brunetti‐Pierri(Federico II University Hospital), Alberto Auricchio(Federico II University Hospital), Raffaella Brunetti‐Pierri(University of Campania "Luigi Vanvitelli"), Rita Ferla(Federico II University Hospital), Maria Vargas(University of Naples Federico II), H. Serap Sivri(Hacettepe University Hospital), Francesca Santamaria(Federico II University Hospital), Mar O’Callaghan(Western University), Francesca Simonelli(University of Naples Federico II), Pierre Romain le Brun(Inserm), Ernesto Soscia(Institute of Biostructure and Bioimaging), Francesco Borgia(Federico II University Hospital), Virginia Maria Ginocchio(Federico II University Hospital), Roberta Romanò(Yale University), Margherita Dell’Anno(Federico II University Hospital), Marco Gargaro(University of Perugia), Giancarlo la Marca(Meyer Children's Hospital), Vincenzo Nigro(University of Campania "Luigi Vanvitelli"), Stefania Galimberti(University of Milano-Bicocca), Francesca Fallarino(University of Perugia), Generoso Andria(Federico II University Hospital), Marialuisa Alliegro(Telethon Institute Of Genetics And Medicine), Stefano Zancan(The San Raffaele Telethon Institute for Gene Therapy), Mafalda Graziano(Telethon Institute Of Genetics And Medicine), Novella Tedesco(Inserm), C. Anthony Rupar(Western University), Giuseppe Servillo(University of Perugia), Alessandro Rossi(Federico II University Hospital), Yılmaz Yıldız(Hacettepe University Hospital), Simona Fecarotta(Federico II University Hospital), P. Véron(Genethon (France)), John J. Mitchell(University of North Carolina at Chapel Hill), Silvia Funghini(Meyer Children's Hospital), Federico Mingozzi(Spark Therapeutics (United States)), Olivier Danos(Regenxbio (United States)), Chitra Prasad(Western University), Maria Grazia Valsecchi(University of Milano-Bicocca), Giancarlo Parenti(European School of Molecular Medicine), Jean‐Brice Marteau(GenoSafe), Valentina Pecorella(Telethon Institute Of Genetics And Medicine)
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