A phase 1 dose escalation study of the pyruvate kinase activator mitapivat (AG-348) in sickle cell disease

Julia Xu(National Institutes of Health), Swee Lay Thein, Emily B. Dunkelberger(National Institutes of Health), Ingrid Frey(National Institutes of Health), Anna Conrey(National Institutes of Health), Laurel A. Menapace(National Institutes of Health), Maureen Lundt(National Institutes of Health), Heidi Mangus(Agios Pharmaceuticals (United States)), Eveline Gwaabe(National Institutes of Health), Penelope A. Kosinski(Agios Pharmaceuticals (United States)), Kristen E. Glass(National Institutes of Health), Peter Hawkins(Agios Pharmaceuticals (United States)), Laxminath Tumburu(National Institutes of Health), Quan Li(National Institutes of Health), Neal Jeffries(National Institutes of Health), William A. Eaton(National Institutes of Health), Charles Kung(Agios Pharmaceuticals (United States)), Timothy Lequang(National Institutes of Health), Varsha Iyer(Agios Pharmaceuticals (United States)), Lenny Dang(Millennium Engineering and Integration (United States))
Blood
May 16, 2022
Cited by 72


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