CRISPR/Cas9 Mediated Gene Modification Ameliorates Abnormal Phenotypes in SCA3/MJD Disease Patient Derived Induced Pluripotent Stem Cells

Lang He(Central South University), Hong Jiang(Central South University), Qi Deng(Central South University), Huifang Zhao(University of Science and Technology of China), Yiqing Gong(Central South University), Guangdong Zou(Central South University), Na Wan(Central South University), Linliu Peng(Central South University), Beisha Tang(Central South University), Linlin Wan(Central South University), Xiaobo Han(Chinese Academy of Sciences), Zhiyuan Li(Guiyang Medical University), Shang Wang(Harbin Institute of Technology), Shuai Li(Zhejiang A & F University), Zhao Chen(Central South University), Yun Peng(Chinese Academy of Sciences), Yue Xie(Central South University), Hongyu Yuan(Central South University), Chunrong Wang(Chinese Center For Disease Control and Prevention), Huirong Peng(Central South University), Lijing Lei(Central South University)
Research Square
October 12, 2020
Cited by 0


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