Home treatment with intravenous enzyme replacement therapy for Gaucher disease: an international collaborative study of 33 patients

A Zimran(Shaare Zedek Medical Center), E Beutler(Shaare Zedek Medical Center), MH van Oers(Amsterdam UMC Location University of Amsterdam), Mark Kelly(Shaare Zedek Medical Center), Aya Abrahamov(Shaare Zedek Medical Center), CE Hollak(Shaare Zedek Medical Center)
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