The effect of enzyme replacement therapy on clinical outcomes in paediatric patients with Fabry disease – A systematic literature review by a European panel of experts

Marco Spada(University of Turin), Dominique P. Germain(Assistance Publique – Hôpitaux de Paris), Bruno Falissard(Inserm), Ralf Baron(Kiel University), Christoph Wanner(Universitätsklinikum Würzburg), Perry Elliott(St Bartholomew's Hospital), Camilla Tøndel(Haukeland University Hospital), Max J. Hilz(Friedrich-Alexander-Universität Erlangen-Nürnberg), Anna Tylki‐Szymańska(Children's Memorial Health Institute), Lorenzo Monserrat(Medical Solutions)
Molecular Genetics and Metabolism
April 26, 2018
10.1016/j.ymgme.2018.04.007
Cited by 81

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