DMD CLINICAL THERAPIES II
Jonathon M. Tinsley(Mary Lyon Centre at MRC Harwell), Kevin Davies(University of Oxford), C. Faelan, Gary Layton(University of Geneva), A. Hetherington, Francesco Muntoni(Great Ormond Street Hospital), J. Patterson-Kane
Cited by 2
Related Papers
Missense Mutations in the Rod Domain of the Lamin A/C Gene as Causes of Dilated Cardiomyopathy and Conduction-System Disease
|New England Journal of Medicine|1999|1.4k
P2X3 receptor antagonist (AF-219) in refractory chronic cough: a randomised, double-blind, placebo-controlled phase 2 study
|The Lancet|2014|488
Mutations in the skeletal muscle α-actin gene in patients with actin myopathy and nemaline myopathy
|Nature Genetics|1999|401
A Randomized, Double-Blind, Placebo-Controlled, Dose-Ranging Study of Oral Sildenafil Citrate in Treatment-Naive Children With Pulmonary Arterial Hypertension
|Circulation|2011|375
CMT subtypes and disease burden in patients enrolled in the Inherited Neuropathies Consortium natural history study: a cross-sectional analysis
|Journal of Neurology Neurosurgery & Psychiatry|2014|342