The effect of enzyme replacement therapy on clinical outcomes in female patients with Fabry disease – A systematic literature review by a European panel of experts

Dominique P. Germain(Assistance Publique – Hôpitaux de Paris), Marco Spada(University of Turin), Derralynn Hughes(Royal Free London NHS Foundation Trust), Michael Arad(Tel Aviv University), Bruno Falissard(Inserm), Christoph Wanner(Universitätsklinikum Würzburg), Frank Weidemann(Katharinenhospital), Max J. Hilz(Friedrich-Alexander-Universität Erlangen-Nürnberg), Alberto Ortíz(Universidad Pontificia de Salamanca), Ulla Feldt‐Rasmussen(Copenhagen University Hospital), Alessandro P. Burlina(Santa Maria Nuova Hospital), Perry Elliott(St Bartholomew's Hospital)
Molecular Genetics and Metabolism
September 27, 2018
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