Gene Therapy Developments for Pompe Disease

Zeenath Unnisa(ProterixBio (United States)), Niek P. van Til(Amsterdam Neuroscience), Jeffrey W. Schindler(Forma Therapeutics (United States)), John K. Yoon(ProterixBio (United States)), Chris Mason(Oak Ridge National Laboratory)
Biomedicines
January 28, 2022
Cited by 51


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