Development of a standard of care for patients with valosin-containing protein associated multisystem proteinopathy

Manisha Kak Korb(University of California, Irvine), Kendrea L. Garand(University of South Alabama), Pradeep P.A. Mammen(The University of Texas Southwestern Medical Center), Ryan Patrick Mahoney, Sujata Patel, Catherine A. Boissoneault, Tanya Stojkovic(Assistance Publique – Hôpitaux de Paris), Miriam Freimer, Mallory Jones, Allison Peck, Elise Healzer, Conrad C. Weihl(Washington University in St. Louis), Stuart H. Ralston(University of Edinburgh), Thomas E. Lloyd(Johns Hopkins University), Ammar Al‐Chalabi(University of Nottingham), Lindsay N. Alfano(Nationwide Children's Hospital), Michael D. Geschwind(University of California, San Francisco), M. James(Newcastle upon Tyne Hospitals NHS Foundation Trust), Bruce L. Miller(University of California, San Francisco), Leo H. Wang, Merrilee Needham, Nita Chen, André Obenaus, Gerald Pfeffer(University of Calgary), Virginia Kimonis(Boston Children's Hospital), Johanna Palmio, Stephani C. Wang, Hani Kushlaf, Katie Kompoliti, S. Ahmad Sajjadi(University of Iowa Hospitals and Clinics), Kenneth I. Berger(Instituto de Biologia Molecular e Celular), Bhaskar Roy(Yale University), Jordi Díaz‐Manera(Hospital de Sant Pau), William W. Seeley(University of California, San Francisco), Margherita Milone(Mayo Clinic in Arizona), Andrea Swenson(The University of Texas at San Antonio Health Science Center), Benison Keung, James Wymer(University of Florida), Roberto D. Fanganiello(Université Laval), Claire Henchcliffe(University of California, Irvine), Rocío‐Nur Villar‐Quiles, Matthew Wicklund(The University of Texas at San Antonio Health Science Center), Nupur Ghoshal, Tahseen Mozaffar(University of North Carolina at Chapel Hill), Betsaida Cruz-Coble, Teresinha Evangelista, Frederick R. Singer(Nottingham City Council), Grace Lee(University of California, Irvine Medical Center), Shaida Khan(The University of Texas Southwestern Medical Center)
Orphanet Journal of Rare Diseases
January 29, 2022
Cited by 36


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