CRISPR/Cas9-based multiplex genome editing of BCL11A and HBG efficiently induces fetal hemoglobin expression

Yuanyuan Han(Western University), Sheng‐Wen Huang(Guizhou Provincial People's Hospital), Xiaoyu Tan(Jiangsu Vocational College of Medicine), Yukio Nakamura(Kyorin University), Hu Li(Guizhou University), Juan Liu(Guizhou University), Di Li(Physical Research Laboratory), Wei Zhang(Hebei North University), Zhaojun Zhang(University of Pennsylvania), Tingting Jin(Soochow University), Siqi Zhao(Chinese Academy of Sciences), Xiangdong Fang(Beijing Institute of Genomics), Ryo Kurita(Japanese Red Cross Society, Japan)
European Journal of Pharmacology
January 28, 2022
Cited by 21


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