Betibeglogene Autotemcel Gene Therapy for Non–β <sup>0</sup> /β <sup>0</sup> Genotype β-Thalassemia

Franco Locatelli(Bambino Gesù Children's Hospital), Mark C. Walters(University of California, San Francisco)

New England Journal of Medicine

December 11, 2021

10.1056/nejmoa2113206

Cited by 251

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