ManNAc Is Safe and Increases Sialic Acid Production in GNE Myopathy (P7.061)
Bradley Class(National Institutes of Health), Nuria Carillo-Carrasco(National Institutes of Health), Frank Celeste(National Institutes of Health), Lea Latham(National Institutes of Health), William A. Gahl(National Institute of Child Health), Marjan Huizing(National Human Genome Research Institute), Amy Wang(National Institutes of Health), Xin Xu(National Institutes of Health), Carla Ciccone(National Institutes of Health), May Christine V. Malicdan(National Institutes of Health)
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