Mitapivat (AG-348) Demonstrates Safety, Tolerability, and Improvements in Anemia, Hemolysis, Oxygen Affinity, and Hemoglobin S Polymerization Kinetics in Adults with Sickle Cell Disease: A Phase 1 Dose Escalation Study
Julia Xu(University of Pittsburgh), Swee Lay Thein(National Heart Lung and Blood Institute), Anna Conrey(National Heart Lung and Blood Institute), Laurel A. Menapace(National Institutes of Health), Maureen Lundt(National Institutes of Health), Heidi Mangus(Agios Pharmaceuticals (United States)), Eveline Gwaabe(National Institutes of Health), Penelope A. Kosinski(Agios Pharmaceuticals (United States)), Kristen E. Glass(National Institutes of Health), Peter Hawkins(Agios Pharmaceuticals (United States)), Laxminath Tumburu(National Heart Lung and Blood Institute), Quan Li(National Institutes of Health), Neal Jeffries(National Institutes of Health), William A. Eaton(National Institutes of Health), Charles Kung(Agios Pharmaceuticals (United States)), Lenny Dang(Millennium Engineering and Integration (United States)), Varsha Iyer(Agios Pharmaceuticals (United States)), Ingrid Frey(National Institutes of Health)
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