584: Delivery of SP-101 restores CFTR function in human CF airway epithelial cultures and drives hCFTRΔR transgene expression in the airways of ferrets
Katherine J. D. A. Excoffon(Roivant Sciences (United States)), R. Kolbeck, M. Glatfelter, Shih-Yao Lin, M. Mahankali, Eric Yuen(Janssen (United States)), Martin Mense(Cystic Fibrosis Foundation), Yanbo Cheng(South China Agricultural University), Mia J. Smith(University of Colorado Denver), Hermann Bihler(Cystic Fibrosis Foundation), Adam D. Werts, B. Gullick, K. Coote, Ziyi Yan(Children's Hospital of Zhejiang University), Philip J. Kuehl, J Engelhardt, Yi Tang(Hunan University of Traditional Chinese Medicine)
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