CRISPR/Cas9 mediated gene correction ameliorates abnormal phenotypes in spinocerebellar ataxia type 3 patient-derived induced pluripotent stem cells

Lang He(Central South University), Hong Jiang(Central South University), Huifang Zhao(University of Science and Technology of China), Jean de Dieu Habimana(Chinese Academy of Sciences), Yiqing Gong(Central South University), Guangdong Zou(Central South University), Na Wan(Central South University), Linliu Peng(Central South University), Beisha Tang(Central South University), Linlin Wan(Central South University), Xiaobo Han(Chinese Academy of Sciences), Zhiyuan Li(Guiyang Medical University), Shang Wang(Harbin Institute of Technology), Shuai Li(Zhejiang A & F University), Zhao Chen(Central South University), Yun Peng(Central South University), Qi Deng(Central South University), Yue Xie(Central South University), Hongyu Yuan(Central South University), Chunrong Wang(Chinese Center For Disease Control and Prevention), Huirong Peng(Central South University), Lijing Lei(Central South University)
Translational Psychiatry
September 17, 2021
Cited by 48


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