Optogenetic modeling of human neuromuscular circuits in Duchenne muscular dystrophy with CRISPR and pharmacological corrections

Amaia Paredes‐Redondo(Queen Mary University of London), Yung‐Yao Lin(Queen Mary University of London), Ivo Lieberam(King's College - North Carolina), Silvia Marino(Queen Mary University of London), Pentao Liu(Hong Kong Science and Technology Parks Corporation), Sandra Louzada(Wellcome Sanger Institute), Anna Kowala(Queen Mary University of London), Jinhong Meng(Great Ormond Street Hospital), Beiyuan Fu(Wellcome Sanger Institute), Olivier Pourquié(Brigham and Women's Hospital), Peter Harley(Queen Mary University of London), Francesco Muntoni(Great Ormond Street Hospital), Jun Wang(Jiangsu Agri-animal Husbandry Vocational College), Eleni Maniati(Queen Mary University of London), David Ryan(University College Cork), Fengtang Yang(Shandong University of Technology)
Science Advances
September 10, 2021
Cited by 19


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