Evaluation of the Humoral Response to Adeno-Associated Virus-Based Gene Therapy Modalities Using Total Antibody Assays

Boris Gorovits(Pfizer (United States)), Bonnie Wu(Janssen (United States)), Mike Havert(Bluebird Bio (United States)), Travis Harrison(Precision for Medicine (United States)), Jim McNally, Mitra Azadeh(Alkermes (United States)), George Buchlis(University of Pennsylvania), Mark Milton(Novartis (United States)), Christian Vettermann(BioMarin (United States)), Robert Nelson, Karen Richards(Precision for Medicine (United States)), Mark Odell(Covance (United States)), Brian Long(BioMarin (United States)), Vibha Jawa(Bristol-Myers Squibb (Germany))
The AAPS Journal
September 16, 2021
10.1208/s12248-021-00628-3
Cited by 52

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