GM1 Gangliosidosis—A Mini-Review

Elena‐Raluca Nicoli(National Institutes of Health), Karolina M. Stępień(Salford Royal NHS Foundation Trust), Cynthia J. Tifft(Children's National), Alessandra d’Azzo(St. Jude Children's Research Hospital), Frances M. Platt(University of Oxford), Ida Annunziata(St. Jude Children's Research Hospital)
Frontiers in Genetics
September 3, 2021
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