Rescue of a lysosomal storage disorder caused by Grn loss of function with a brain penetrant progranulin biologic

Todd Logan(Denali Therapeutics (United States)), Matthew Simon(Denali Therapeutics (United States)), Anil Rana(Denali Therapeutics (United States)), Gerald Maxwell Cherf(Denali Therapeutics (United States)), Ankita Srivastava(Denali Therapeutics (United States)), Sonnet S. Davis(Denali Therapeutics (United States)), Ray Low(Denali Therapeutics (United States)), Chi‐Lu Chiu(Denali Therapeutics (United States)), Meng Fang(Denali Therapeutics (United States)), Fen Huang(Denali Therapeutics (United States)), Akhil Bhalla(Denali Therapeutics (United States)), Ceyda Llapashtica(Denali Therapeutics (United States)), Rachel Prorok(Denali Therapeutics (United States)), Michelle E. Pizzo(Denali Therapeutics (United States)), Meredith Calvert(Denali Therapeutics (United States)), Elizabeth W. Sun(Denali Therapeutics (United States)), Jennifer Hsiao‐Nakamoto(Denali Therapeutics (United States)), Yashas Rajendra(Denali Therapeutics (United States)), Katrina W. Lexa(Denali Therapeutics (United States)), Devendra B. Srivastava(Denali Therapeutics (United States)), Bettina van Lengerich(Denali Therapeutics (United States)), Junhua Wang(Denali Therapeutics (United States)), Yaneth Robles‐Colmenares(Denali Therapeutics (United States)), Do Jin Kim(Denali Therapeutics (United States)), Joseph Duque(Denali Therapeutics (United States)), Melina Lenser(Denali Therapeutics (United States)), Timothy Earr(Denali Therapeutics (United States)), Hoang N. Nguyen(Denali Therapeutics (United States)), Roni Chau(Denali Therapeutics (United States)), Buyankhishig Tsogtbaatar(Denali Therapeutics (United States)), Ritesh Ravi(Denali Therapeutics (United States)), Lukas L. Skuja(Denali Therapeutics (United States)), Hilda Solanoy(Denali Therapeutics (United States)), Howard J. Rosen(University of California, San Francisco), Bradley F. Boeve(Mayo Clinic), Adam L. Boxer(University of California, San Francisco), Hilary W. Heuer(University of California, San Francisco), Mark S. Dennis(Denali Therapeutics (United States)), Mihalis S. Kariolis(Denali Therapeutics (United States)), Kathryn M. Monroe(Denali Therapeutics (United States)), Laralynne Przybyla(Denali Therapeutics (United States)), Pascal E. Sanchez(Denali Therapeutics (United States)), René Meisner(Denali Therapeutics (United States)), Dolores Diaz(Denali Therapeutics (United States)), Kirk R. Henne(Denali Therapeutics (United States)), Ryan J. Watts(Denali Therapeutics (United States)), Anastasia G. Henry(Denali Therapeutics (United States)), Kannan Gunasekaran(Denali Therapeutics (United States)), Giuseppe Astarita(Georgetown University), Jung H. Suh(Denali Therapeutics (United States)), Joseph W. Lewcock(Denali Therapeutics (United States)), Sarah L. DeVos(Denali Therapeutics (United States)), Gilbert Di Paolo(Denali Therapeutics (United States))
Cell
August 26, 2021
Cited by 226Open Access
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