The comparison of ZFNs, TALENs, and SpCas9 by GUIDE-seq in HPV-targeted gene therapy
Zifeng Cui(Sun Yat-sen University), Hui Liu, Hongfeng Zhang(Central Hospital of Wuhan), Zhaoyue Huang(Sun Yat-sen University), Rui Tian(Sun Yat-sen University), Lifang Li(Sun Yat-sen University), Weiwen Fan(Sun Yat-sen University), Yili Chen(Sun Yat-sen University), Lijie Chen(Bengbu Medical College), Sen Zhang(Bengbu Medical College), Bhudev C. Das(Amity University), Konstantin Severinov(Skolkovo Institute of Science and Technology), Inga I. Hitzeroth(University of Cape Town), Priya Ranjan Debata(Maharaja Sriram Chandra Bhanja Deo University), Zhuang Jin(Sun Yat-sen University), Jiashuo Liu(Sun Yat-sen University), Zheying Huang(Sun Yat-sen University), Weiling Xie(Sun Yat-sen University), Hongxian Xie(Guangzhou Regenerative Medicine and Health Guangdong Laboratory), Bin Lang(Macao Polytechnic University), Ji Ma(Suizhou Central Hospital), Haiyan Weng(University of Science and Technology of China), Xun Tian(Central Hospital of Wuhan), Zheng Hu(Sun Yat-sen University)
Cited by 51Open Access
Abstract
off-target detection pipeline for three generations of artificial nucleases provided useful tools for genome engineering-based gene therapy.
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