Base editing of haematopoietic stem cells rescues sickle cell disease in mice

Gregory A. Newby(Broad Institute), Jonathan Yen(St. Jude Children's Research Hospital), Kaitly J. Woodard(St. Jude Children's Research Hospital), Thiyagaraj Mayuranathan(St. Jude Children's Research Hospital), Cícera R. Lazzarotto(St. Jude Children's Research Hospital), Yichao Li(St. Jude Children's Research Hospital), Heather Sheppard(St. Jude Children's Research Hospital), Shaina N. Porter(St. Jude Children's Research Hospital), Yu Yao(St. Jude Children's Research Hospital), Kalin Mayberry(St. Jude Children's Research Hospital), Kelcee A. Everette(Broad Institute), Yoonjeong Jang(St. Jude Children's Research Hospital), Christopher J. Podracky(Broad Institute), Elizabeth Thaman(Cincinnati Children's Hospital Medical Center), Christophe Lechauve(St. Jude Children's Research Hospital), Akshay Sharma(St. Jude Children's Research Hospital), Jordana M. Henderson(TriLink BioTechnologies (United States)), Michelle F. Richter(Broad Institute), Kevin T. Zhao(Broad Institute), Shannon M. Miller(Broad Institute), Tina Wang(Broad Institute), Luke W. Koblan(Broad Institute), Anton P. McCaffrey(TriLink BioTechnologies (United States)), John F. Tisdale(National Institute of Diabetes and Digestive and Kidney Diseases), Theodosia A. Kalfa(Cincinnati Children's Hospital Medical Center), Shondra M. Pruett‐Miller(St. Jude Children's Research Hospital), Shengdar Q. Tsai(St. Jude Children's Research Hospital), Mitchell J. Weiss(St. Jude Children's Research Hospital), David R. Liu(Broad Institute)
Nature
June 2, 2021
Cited by 375Open Access
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