Natural gene therapy by reverse mosaicism leads to improved hematology in <scp>Fanconi</scp> anemia patients
Marı́a José Ramı́rez(Universitat Autònoma de Barcelona), Jordi Surrallés(Universitat Autònoma de Barcelona), Albert Català(Hospital Sant Joan de Déu Barcelona), Bienvenida Argilés, Cristina Beléndez(Hospital General Universitario Gregorio Marañón), Isabel Badell(Hospital de Sant Pau), Susana Navarro(Centre for Biomedical Network Research on Rare Diseases), Estela Carrasco(Vall d'Hebron Hospital Universitari), Cristina Díaz de Heredia(Universitat Autònoma de Barcelona), Julián Sevilla(University of Southern Denmark), Paula Rı́o(Centre for Biomedical Network Research on Rare Diseases), José Antonio Casado(Centre for Biomedical Network Research on Rare Diseases), Jordi Minguillón(Universitat Pompeu Fabra), Judith Balmañà(Vall d'Hebron Hospital Universitari), Jonathan D. Schwartz(Temple University), Massimo Bogliolo(Universitat Autònoma de Barcelona), Eileen Nicoletti(Sunesis (United States)), Monica López(Hospital Universitari Joan XXIII de Tarragona), Roser Pujol(Universitat Autònoma de Barcelona), Juan Pablo Trujillo‐Quintero(Universidade da Coruña), Gayatri R Rao(Sunesis (United States)), Juan A. Bueren(Centro de Investigación Biomédica en Red)
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