Health economic burden of patients with phenylketonuria (PKU) – A retrospective study of German health insurance claims data

Friedrich K. Trefz(University Medical Center Groningen), Frank Rutsch(Klinik und Poliklinik für Kinder- und Jugendmedizin), J. Altevers, Ania C. Muntau(University Medical Center Hamburg-Eppendorf), Claudia Zeiss, Ashok Kumar Jha(BioMarin (United Kingdom)), Sebastian Braun(Goethe University Frankfurt), Paul Lane(BioMarin (United Kingdom)), Christian Jacob, Mohit Jain(BioMarin (United Kingdom)), Ignacio Alvarez(BioMarin (United Kingdom)), Kim Maren Schneider, Wolfgang Greiner(Bielefeld University)
Molecular Genetics and Metabolism Reports
May 13, 2021
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