Merosin deficient congenital muscular dystrophy type 1A: An international workshop on the road to therapy 15-17 November 2019, Maastricht, the Netherlands

Hubert J.M. Smeets(Maastricht University), Teun van Zutphen(Maastricht University), Nicol C. Voermans(Radboud University Nijmegen), Andrea Klein(University Children's Hospital Zurich), Giulio Cossu(Vita-Salute San Raffaele University), Marie-Julie D K Lemmens(Maastricht University), Gustavo Dziewczapolski(Cure CMD), Corrie E. Erasmus(Radboud University Medical Center), Madeleine Durbeej(Lund University), Reghan Foley(National Institutes of Health), Leonardo Zingler Herrero(Maastricht University), Dwi U. Kemaladewi(University of Pittsburgh), Anna Sárközy(Great Ormond Street Hospital), Markus A. Rüegg(University of Basel), Florence van Tienen(Maastricht University Medical Centre), Hemant Sawnani(University of Cincinnati), Maurilio Sampaolesi(Sapienza University of Rome), Bram Verbrugge, Pierre Springuel(Maastricht University), I.F.M. de Coo(Maastricht University), Haluk Topaloğlu(Yeditepe University), Sweta Girgenrath(University of Massachusetts Chan Medical School), Dirk Jan Stelwagen, Heleen Stelwagen(Dialyse Centrum Groningen), Eric Dragendorf(Maastricht University), Christos Diamantidis(Maastricht University), Lotte van de Loo(Maastricht University), Peter D. Yurchenco(Rutgers, The State University of New Jersey), Anas S. Said(Maastricht University), Stefano C. Previtali(Vita-Salute San Raffaele University)
Neuromuscular Disorders
May 1, 2021
Cited by 7


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