Use of single guided Cas9 nickase to facilitate precise and efficient genome editing in human iPSCsPan P. Li(Johns Hopkins University), Russell L. Margolis(Johns Hopkins University)Scientific ReportsMay 10, 202110.1038/s41598-021-89312-2Cited by 15SaveCiteExport RISWatch citationsRelated PapersEffect of Deutetrabenazine on Chorea Among Patients With Huntington Disease|JAMA|2016|397A randomized, double-blind, placebo-controlled trial of coenzyme Q10 in Huntington disease|Neurology|2016|137Effect of Deutetrabenazine on Chorea Among Patients With Huntington Disease A Randomized Clinical Trial|Publisher|2016|44A randomized, double-blind, placebo-controlled trial of coenzyme Q10 in Huntington disease|Unknown|2017|28