Widespread and sustained target engagement in Huntington’s disease minipigs upon intrastriatal microRNA-based gene therapy
Astrid Vallès(UniQure (Netherlands)), Pavlina Konstantinova(Io Therapeutics (United States)), Jiřı́ Klı́ma(Czech Academy of Sciences, Institute of Animal Physiology and Genetics), Michal Crha(University of Veterinary Sciences Brno), Anouk Stam(UniQure (Netherlands)), Seyda Acar-Broekmans(UniQure (Netherlands)), Roberta Pintauro(IRBM Science Park), Harald Petry(UniQure (Netherlands)), Dušan Urgošík(Na Homolce Hospital), Božena Bohuslavová(Czech Academy of Sciences, Institute of Animal Physiology and Genetics), Cynthia Brouwers(UniQure (Netherlands)), Zdeňka Ellederová(Czech Academy of Sciences, Institute of Animal Physiology and Genetics), Zdeněk Stárek(St. Anne's University Hospital Brno), Bas Blits(Tilburg University), Melvin M. Evers(UniQure (Netherlands)), Alberto Bresciani(University of Bergamo), Valentina Fodale(IRBM Science Park), Carlos Vendrell‐Tornero(UniQure (Netherlands)), Marina Sogorb-González(Io Therapeutics (United States)), Sander van Deventer(UniQure (Netherlands)), Lieke Paerels(UniQure (Netherlands)), Jan Motlík(Czech Academy of Sciences, Institute of Animal Physiology and Genetics), Roman Liščák(Na Homolce Hospital)
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