Morquio A syndrome and effect of enzyme replacement therapy in different age groups of Turkish patients: a case series

Sebile Kılavuz(Ministry of Health), Neslihan Önenli Mungan(Cukurova University), Sibel Başaran(Cukurova University), Atıl Bişgin(Cukurova University), Fatma Derya Bulut(Cukurova University), Muhammed Dağkıran(Cukurova University), Deniz Kör(Cukurova University), Sevcan Erdem(Cukurova University), Hüseyin Tuğsan Ballı(Cukurova University)
Orphanet Journal of Rare Diseases
March 22, 2021
Cited by 11


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