Cas9 protein delivery non-integrating lentiviral vectors for gene correction in sickle cell disease

Naoya Uchida(National Heart Lung and Blood Institute), John F. Tisdale(National Institutes of Health), Jackson Gamer(National Institute of Diabetes and Digestive and Kidney Diseases), Selami Demirci(National Heart Lung and Blood Institute), Yoshitaka SHIBATA(National Institutes of Health), Juan J. Haro‐Mora(National Institutes of Health), Claire Drysdale(National Institute of Diabetes and Digestive and Kidney Diseases), Tina Nassehi(National Institute of Diabetes and Digestive and Kidney Diseases), Morgan Yapundich(National Institute of Diabetes and Digestive and Kidney Diseases), Malikiya Hinds(National Institutes of Health), Julia DiNicola(National Institutes of Health)
Molecular Therapy — Methods & Clinical Development
March 2, 2021
Cited by 51


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