Decreased activity and stability of pyruvate kinase in sickle cell disease: a novel target for mitapivat therapy
Minke A.E. Rab(Utrecht University), Richard van Wijk(Utrecht University), Hyeryun Kim(Agios Pharmaceuticals (United States)), Gerard Pasterkamp(University Medical Center Utrecht), Victor Chubukov(Agios Pharmaceuticals (United States)), Heidi Mangus(Agios Pharmaceuticals (United States)), Penelope A. Kosinski(Agios Pharmaceuticals (United States)), Roger E. G. Schutgens(University Medical Center Utrecht), Stephanie van Straaten(Utrecht University), Brigitte A. van Oirschot(Utrecht University), Jennifer Bos(Utrecht University), Lenny Dang(Millennium Engineering and Integration (United States)), Charles Kung(Agios Pharmaceuticals (United States)), Eduard J. van Beers(Utrecht University)
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