Long-term safety and efficacy of tezacaftor–ivacaftor in individuals with cystic fibrosis aged 12 years or older who are homozygous or heterozygous for Phe508del CFTR (EXTEND): an open-label extension study

Patrick A. Flume(Medical University of South Carolina), Reta Fischer Biner(Lindenhofspital), D.G. Downey(Queen's University Belfast), Cynthia D. Brown(Northwestern University), Manu Jain(Northwestern University), Rainald Fischer(Orthopädische Praxis), K. De Boeck(Boston Children's Hospital), Gregory S. Sawicki(Boston Children's Hospital), Philip M. Chang(Vertex Pharmaceuticals (United States)), Hildegarde Paz-Díaz(Vertex Pharmaceuticals (United States)), Jaime Rubin(Vertex Pharmaceuticals (United States)), Yoojung Yang(Vertex Pharmaceuticals (United States)), Xingdi Hu(Pinnacle Clinical Research), David J. Pasta(Pinnacle Clinical Research), Stefanie J. Millar(Pinnacle Clinical Research), Daniel Campbell(United States Food and Drug Administration), Xin Wang(Vertex Pharmaceuticals (United States)), Neil Ahluwalia(Vertex Pharmaceuticals (United States)), Caroline A. Owen(The University of Queensland), Claire Wainwright(The University of Queensland), Ronald L. Gibson, Steven M. Rowe, Noah Lechtzin, Richard C. Ahrens, Karen McCoy, Moira L. Aitken, Scott H. Donaldson, Kimberly McBennett, Joseph M. Pilewski, Joanne Billings(Pinnacle Clinical Research), Carlos Milla, Ronald C. Rubenstein, Daniel Rosenbluth, Rachel W. Linnemann, Michael R. Powers, Christopher N. Fortner, Carla A. Frederick, Theodore G. Liou(Vertex Pharmaceuticals (United States)), Philip Black(United States Food and Drug Administration), Janice Wang, John L. Colombo, Maria Berdella, M.V. Indihar(Indiana University School of Medicine), Cynthia D. Brown(Indiana University School of Medicine), Michael Anstead, Lara Bilodeau, Leonard Sicilian(Northwestern University), Manu Jain(Northwestern University), James Tolle, Kathryn Moffett, Samya Z. Nasr, Jennifer L. Taylor‐Cousar, Tara Lynn Barto, Nicholas Antos, John Rogers, Bryon Quick, Henry R. Thompson(Boston Children's Hospital), Gregory S. Sawicki(Boston Children's Hospital), Bruce Barnett, Robert Zanni, Thomas C. Smith, Karen D. Schultz(The University of Queensland), Claire Keating(Medical University of South Carolina), Patrick A. Flume(Medical University of South Carolina), Gregory J. Omlor, Alix Ashare, Karen Z. Voter, Nighat Mehdi, Maria Gabriela Tupayachi Ortiz, Tonia E. Gardner, Steven R. Boas, Barbara Messore, Edith T. Zemanick(Northwestern University), Raksha Jain, Michael McCarthy, Dana G. Kissner, K. Patel, John McNamara, Julie V. Philley, Ariel Berlinski, Francisco J. Calimano, Terry Chin, Douglas Conrad, Cori Daines, Hengameh Raissy, Thomas G. Keens, Jorge Lascano, Bennie McWilliams, Brian Morrissey, Santiago Reyes, Subramanyam Chittivelu, Sabiha Hussain, Arvey Stone, James Wallace, Ross C. Klingsberg, Julie Biller, S. Bui, Olaf Sommerburg, Elisabetta Bignamini, Mirella Collura(Lindenhofspital), Reta Fischer Biner(Lindenhofspital), Alexander Mœller, Donatello Salvatore, C. Belleguic, Lea Bentur, Ori Efrati, Eitan Kerem, Dario Prais, Esther Quintana‐Gallego, Peter J. Barry, Galit Livnat-Levanon, José Ramón Villa Asensi, David Armstrong, Oscar A. Cruz, Francis Gilchrist, D. Elizabeth Tullis, Bradley S. Quon, Larry C. Lands, Nancy Morrison, Annick Lavoie, Barry Linnane, Okan Elidemir, Felix C. Ringshausen, Matthias Kappler, Helge Hebestreit, Jochen G. Mainz, Alexander Kiefer, Cordula Koerner‐Rettberg, Doris Staab, Wolfgang Gleiber, Tacjana Pressler, Florian Stehling, Andreas Hector, Sivagurunathan Sutharsan, Lutz Naehrlich(Orthopädische Praxis), Rainald Fischer(Queen's University Belfast), D.G. Downey(Queen's University Belfast), Jane C. Davies, R.I. Ketchell, Mary P. Carroll, Simon Doe, Gordon MacGregor, E.F. Nash, Nicholas Withers, D. Peckham, M.J. Ledson, Sonal Kansra, Timothy William Rayner Lee, Bertrand Delaisi, G. Rault, Jean Le Bihan, D. Hubert, Isabelle Fajac, Isabelle Sermet‐Gaudelus, Marleen Bakker, Bert Arets(KU Leuven), Christiane De Boeck, R. Chiron, Philippe Reix, Catherine Mainguy, Eva Van Braeckel, Anne Malfroot, I. Durieu, Nadine Dufeu, Anne Prévötat, Renske van der Meer, Petrus Merkus(Pinnacle Clinical Research), Els J.M. Weersink, Isabel Barrio Gomez-Aguero, Silvia Gärtner, Amparo Sole Jover, Antonio Álvarez Fernández, D. Cox, Edward F. McKone, Barry J. Plant, Hiranjan Selvadurai, Simon Bowler(The University of Queensland), Claire Wainwright(The University of Queensland), Daniel J. Smith, Peter G. Middleton, John Wilson, Sonia Volpi, Carla Colombo, Benedetta Fabrizzi, V. Lucidi, Federico Cresta, Salvatore Cucchiara, Ernst Eber, Helmut Ellemunter, Isidor Huttegger, Lena Hjelte, Christina Krantz, Marita Gilljam
The Lancet Respiratory Medicine
February 10, 2021
Cited by 51Open Access
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