Prednisolone rescues Duchenne muscular dystrophy phenotypes in human pluripotent stem cell–derived skeletal muscle in vitro

Ziad Al Tanoury(Brigham and Women's Hospital), Olivier Pourquié(Brigham and Women's Hospital), Harold M. McNamara(Princeton University), Vandana Gupta(Brigham and Women's Hospital), Svetlana Gapon(Brigham and Women's Hospital), Rhonda Bassel‐Duby(The University of Texas Southwestern Medical Center), John F. Zimmerman(Harvard University), Bianca Habermann(Max Planck Institute of Molecular Cell Biology and Genetics), Kevin Kit Parker(Harvard University), Daniel Sieiro(Brigham and Women's Hospital), Thomas Cherrier(Université de Strasbourg), Jyoti Rao(Brigham and Women's Hospital), Jérome Chal(Stowers Institute for Medical Research), Fabio Marchianò(Centre National de la Recherche Scientifique), Charlotte Fugier-Schmucker, Adam E. Cohen(Harvard University), Aurore Hick-Colin, Alejandra Rodríguez‐delaRosa(Brigham and Women's Hospital), Eric N. Olson(Southwestern Medical Center), Alexander P. Nesmith(Harvard University), Fanny Bousson, Erica Wagner(Brigham and Women's Hospital)
Proceedings of the National Academy of Sciences
July 6, 2021
Cited by 72


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