ACCELERATE: A Patient-Powered Natural History Study Design Enabling Clinical and Therapeutic Discoveries in a Rare Disorder
Sheila K. Pierson(University of Pittsburgh Medical Center), David C. Fajgenbaum(University of Pennsylvania), Faizaan Akhter(University of Pennsylvania), Simone Ferrero(Azienda Ospedaliera Citta' della Salute e della Scienza di Torino), Jason R. Ruth(University of Pennsylvania), Katherine Floess(University of Pennsylvania), Kojo S.J. Elenitoba‐Johnson(Memorial Sloan Kettering Cancer Center), Raj Jayanthan(Baylor College of Medicine), J.L. Patier de la Peña(Instituto Ramón y Cajal de Investigación Sanitaria), Megan S. Lim(Memorial Sloan Kettering Cancer Center), Johnson S. Khor(University of Pennsylvania), Alexander Gorzewski(University of Pennsylvania), Thomas S. Uldrick(Regeneron (United States)), Louis Terriou(Centre Hospitalier Universitaire de Lille), Alexander Fosså(Oslo University Hospital), Matthew Streetly(King's College - North Carolina), Bette Jacobs, Amy Chadburn(Cornell University), Erin Napier(University of Pennsylvania), Gordan Srkalović(Regional Cancer Center), Mark-Avery Tamakloe(University of Pennsylvania), Jasira Ziglar(University of Pennsylvania), Linus Angenendt(Board of the Swiss Federal Institutes of Technology), Mileva Repasky, Corey Casper(University of Washington), Eric Haljasmaa(University of Pennsylvania), Elaine S. Jaffe(National Cancer Institute), Frits van Rhee(Winthrop Rockefeller Foundation), Pier Luigi Zinzani(Istituto di Ematologia di Bologna), Amy Liu(University of California San Diego), Christian Hoffmann(Hochschule für Angewandte Wissenschaften Kiel), Victoria Powers(University of Pennsylvania), Arthur H. Rubenstein(University of Pennsylvania), Éric Oksenhendler(Université Paris Cité)
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