Long‐term disease course of two patients with multiple sulfatase deficiency differs from metachromatic leukodystrophy in a broad cohort
Stefanie Beck‐Wödl(University of Tübingen), Judith Böhringer(University Children's Hospital Tübingen), K. Harzer(University of Tübingen), Dorothea Haas(Heidelberg University), Samuel Groeschel(University of Tübingen), Ingeborg Krägeloh‐Mann(University Children's Hospital Tübingen), Christiane Kehrer(University Children's Hospital Tübingen), Angelika Rieß(University of Tübingen), Friederike Bürger(Boston Children's Hospital), Tobias B. Haack(Technical University of Munich)
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