Effectiveness and safety of the tri-iodothyronine analogue Triac in children and adults with MCT8 deficiency: an international, single-arm, open-label, phase 2 trial
Stefan Groeneweg(Erasmus University Rotterdam), Visser WE, Oliver Petit, Athanasia Stoupa(Hôpital Necker-Enfants Malades), De Meirleir L, Jan Lebl(Charles University), P Vrijmoeth, Dana Craiu, Bertini ES(University of Zurich), Nicole I. Wolf(Emma Kinderziekenhuis), Marco Medici(Radboud University Nijmegen), Sylvia Depoorter(AZ Sint-Jan), Davide Tonduti, Federica Zibordi(Fondazione IRCCS Istituto Neurologico Carlo Besta), Marco Cappa(Bambino Gesù Children's Hospital), RJ Lunsing(University of Zurich), de Coo IFM(University of Zurich), Angelique Zandstra, Visser FE, Anne McGowan(University of Cambridge), Yanglem Ajitkumar Singh, S Nowak(Refaja Ziekenhuis), Klára Roženková(Charles University), den Uil CA, Robin P. Peeters(Unknown), van Beynum Im(University of Zurich), Diana Bârcă(Clinical Emergency Hospital Bucharest), Carolina Morán(Cambridge University Hospitals NHS Foundation Trust), K Chatterjee, Martien Manshande('s Heeren Loo), Heiko Krude(Humboldt-Universität zu Berlin), J. R. C. Jansen, de Rijke Yb, FK Aarsen, de Wit MCY, van der Walt A, van der Knoop(Erasmus MC - Sophia Children’s Hospital), Laura Paone(Bambino Gesù Children's Hospital), Zillikens MC, M. Polak, Visser Tj, Jana Malíková(Charles University), G Lyons(University of Zurich), Gautam Ambegaonkar(Cambridge University Hospitals NHS Foundation Trust), F Auriol, Alice Dica(Spitalul Clinic de Psihiatrie Alexandru Obregia)
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