Restoration of visual function in adult mice with an inherited retinal disease via adenine base editing

Susie Suh(University of California, Irvine), Elliot H. Choi(University of California, Irvine), Henri Leinonen(University of California, Irvine), Andrzej T. Foik(University of California, Irvine), Gregory A. Newby(Broad Institute), Wei-Hsi Yeh(Broad Institute), Zhiqian Dong(University of California, Irvine), Philip D. Kiser(University of California, Irvine), David C. Lyon(University of California, Irvine), David R. Liu(Broad Institute), Krzysztof Palczewski(University of California, Irvine)
Nature Biomedical Engineering
October 19, 2020
Cited by 167Open Access
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