BCL11A enhancer–edited hematopoietic stem cells persist in rhesus monkeys without toxicity

Selami Demirci(National Institutes of Health), John F. Tisdale(National Heart Lung and Blood Institute), Anne H. Shen(Broad Institute), Jackson Gamer(National Institute of Diabetes and Digestive and Kidney Diseases), Scot A. Wolfe(University of Massachusetts Chan Medical School), Nathaniel S. Linde(National Institutes of Health), Shondra M. Pruett‐Miller(St. Jude Children's Research Hospital), Aylin Bonifacino(National Institutes of Health), Alexis Leonard(St. Jude Children's Research Hospital), Naoya Uchida(National Heart Lung and Blood Institute), Yuxuan Wu(Qufu Normal University), Juan J. Haro‐Mora(National Institutes of Health), Claire Drysdale(National Institute of Diabetes and Digestive and Kidney Diseases), Theresa Engels(National Institutes of Health), Cícera R. Lazzarotto(St. Jude Children's Research Hospital), Jing Zeng(Broad Institute), Kevin Luk(University of Massachusetts Chan Medical School), Mitchell J. Weiss(St. Jude Children's Research Hospital), Tina Nassehi(National Institute of Diabetes and Digestive and Kidney Diseases), Morgan Yapundich(National Institute of Diabetes and Digestive and Kidney Diseases), Daniel E. Bauer(Broad Institute), Jasmine Bonanno(Dana-Farber Cancer Institute), Robert E. Donahue(National Institute of Diabetes and Digestive and Kidney Diseases), Danilo Pellin(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Allen E. Krouse(National Institutes of Health), Shengdar Q. Tsai(Harvard University), Shaina N. Porter(St. Jude Children's Research Hospital)
Journal of Clinical Investigation
September 8, 2020
Cited by 67


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