Gene Therapy Preserves Retinal Structure and Function in a Mouse Model of NMNAT1-Associated Retinal Degeneration
Scott H. Greenwald(Massachusetts Eye and Ear Infirmary), Eric A. Pierce(Broad Institute), Michael J. Scandura(Massachusetts Eye and Ear Infirmary), Raymond Farmer(Massachusetts Eye and Ear Infirmary), Erin Hennessey(Massachusetts Eye and Ear Infirmary), Ru Xiao(Anhui University of Traditional Chinese Medicine), Luk H. Vandenberghe(Massachusetts Eye and Ear Infirmary), Basil S. Pawlyk(Berman Center for Outcomes and Clinical Research), Emily E. Brown(Massachusetts Eye and Ear Infirmary)
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