IgG-cleaving endopeptidase enables in vivo gene therapy in the presence of anti-AAV neutralizing antibodies

Christian Leborgne(Inserm), Elena Barbon(Inserm), J M Alexander(Spark Therapeutics (United States)), Hayley A. Hanby(Spark Therapeutics (United States)), Sandrine Delignat(Inserm), Daniel M. Cohen(Spark Therapeutics (United States)), Fanny Collaud(Inserm), Saghana Muraleetharan(Spark Therapeutics (United States)), Dan Lupo(Spark Therapeutics (United States)), Joseph Silverberg(Spark Therapeutics (United States)), Karen Huang(Spark Therapeutics (United States)), Laetitia van Wittengerghe(Inserm), Béatrice Marolleau(Inserm), Adeline Miranda(Inserm), Anna Fabiano(Inserm), Victoria Daventure(Inserm), Heena Beck(Spark Therapeutics (United States)), Xavier M. Anguela(Spark Therapeutics (United States)), Giuseppe Ronzitti(Inserm), Sean M. Armour(Spark Therapeutics (United States)), Sébastien Lacroix‐Desmazes(Université Paris Cité), Federico Mingozzi(Université Paris-Saclay)
Nature Medicine
June 1, 2020
Cited by 311Open Access
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