Subacute Liver Failure Following Gene Replacement Therapy for Spinal Muscular Atrophy Type 1

Amy G. Feldman(Children's Hospital Colorado), Julie Parsons(Children's Hospital Colorado), Cullen M. Dutmer(Children's Hospital Colorado), Aravindhan Veerapandiyan(Arkansas Children's Hospital), Einar Hafberg(Monroe Carell Jr. Children's Hospital), Nolan Maloney(University of Colorado Denver), Cara L. Mack(Children's Hospital Colorado)
The Journal of Pediatrics
May 27, 2020
Cited by 132Open Access
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