Brain delivery and activity of a lysosomal enzyme using a blood-brain barrier transport vehicle in mice
Julie C. Ullman(Denali Therapeutics (United States)), Annie Arguello(Denali Therapeutics (United States)), Jennifer A. Getz(Denali Therapeutics (United States)), Akhil Bhalla(Denali Therapeutics (United States)), Cathal Mahon(Denali Therapeutics (United States)), Junhua Wang(Denali Therapeutics (United States)), Tina Giese(Denali Therapeutics (United States)), Catherine Bédard(Denali Therapeutics (United States)), Do Jin Kim(Denali Therapeutics (United States)), Jessica Blumenfeld(Denali Therapeutics (United States)), Nicholas Liang(Denali Therapeutics (United States)), Ritesh Ravi(Denali Therapeutics (United States)), Alicia Nugent(Denali Therapeutics (United States)), Sonnet S. Davis(Denali Therapeutics (United States)), Connie Ha(Denali Therapeutics (United States)), Joseph Duque(Denali Therapeutics (United States)), Hai L. Tran(Denali Therapeutics (United States)), Robert C. Wells(Denali Therapeutics (United States)), Steve Lianoglou(Denali Therapeutics (United States)), Vinay M. Daryani(Denali Therapeutics (United States)), Wanda Kwan(Denali Therapeutics (United States)), Hilda Solanoy(Denali Therapeutics (United States)), Hoang N. Nguyen(Denali Therapeutics (United States)), Timothy Earr(Denali Therapeutics (United States)), Jason C. Dugas(Denali Therapeutics (United States)), Michael Tuck(Vanderbilt University), Jennifer Harvey(Vanderbilt University), Michelle L. Reyzer(Vanderbilt University), Richard M. Caprioli(Vanderbilt University), Sejal S. Hall(Denali Therapeutics (United States)), Suresh B. Poda(Denali Therapeutics (United States)), Pascal E. Sanchez(Denali Therapeutics (United States)), Mark S. Dennis(Denali Therapeutics (United States)), Kannan Gunasekaran(Denali Therapeutics (United States)), Ankita Srivastava(Denali Therapeutics (United States)), Thomas Sandmann(Denali Therapeutics (United States)), Kirk R. Henne(Denali Therapeutics (United States)), Robert G. Thorne(Denali Therapeutics (United States)), Gilbert Di Paolo(Denali Therapeutics (United States)), Giuseppe Astarita(Denali Therapeutics (United States)), Dolores Diaz(Denali Therapeutics (United States)), Adam P. Silverman(Denali Therapeutics (United States)), Ryan J. Watts(Denali Therapeutics (United States)), Zachary K. Sweeney(Denali Therapeutics (United States)), Mihalis S. Kariolis(Denali Therapeutics (United States)), Anastasia G. Henry(Denali Therapeutics (United States))
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Abstract
An enzyme transport vehicle enables brain delivery of lysosomal enzymes across the blood-brain barrier in mice.
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