Applying genome-wide CRISPR-Cas9 screens for therapeutic discovery in facioscapulohumeral muscular dystrophy
Angela Lek(Muscular Dystrophy Association), Louis M. Kunkel(Boston Children's Hospital), Monkol Lek(Massachusetts General Hospital), Peter L. Jones(University of Nevada, Reno), Alec M. DeSimone(University of Massachusetts Chan Medical School), Anna Pakuła(Boston Children's Hospital), Keryn G. Woodman(Yale University), Tracy Zhang(Boston Children's Hospital), Andrew Kodani(University of California, San Francisco), Lillian Mead(Boston Children's Hospital), Oliver D. King(Boston Biomedical Research Institute), Shushu Huang(Yale University), Justin Cohen(Yale University), James R. Conner(Boston Children's Hospital), Vincent Ho(Yale University), Kathryn R. Wagner(Kennedy Krieger Institute), Neville E. Sanjana(New York Genome Center)
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