Human iPSC-based neurodevelopmental models of globoid cell leukodystrophy uncover patient- and cell type-specific disease phenotypes

Elisabeth Mangiameli(The San Raffaele Telethon Institute for Gene Therapy), Angela Gritti(The San Raffaele Telethon Institute for Gene Therapy)
bioRxiv (Cold Spring Harbor Laboratory)
March 15, 2020
Cited by 0


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