Combined Treatment with Peptide-Conjugated Phosphorodiamidate Morpholino Oligomer-PPMO and AAV-U7 Rescues the Severe DMD Phenotype in Mice
Anne Forand(Inserm), France Piétri‐Rouxel(Inserm), Charlotte Izabelle(Centre National de la Recherche Scientifique), Caroline Sévoz‐Couche(Inserm), Nathalie Mougenot(Inserm), Cécile Peccate(Inserm), Matthew J. A. Wood(University of Oxford), Antoine Muchir(Inserm), Mégane Lemaître(Inserm), Stéphanie Lorain(Inserm)
Cited by 22
Related Papers
Mandibuloacral Dysplasia Is Caused by a Mutation in LMNA-Encoding Lamin A/C
|The American Journal of Human Genetics|2002|534
Activation of MAPK pathways links LMNA mutations to cardiomyopathy in Emery-Dreifuss muscular dystrophy
|Journal of Clinical Investigation|2007|303
Amelioration of systemic inflammation via the display of two different decoy protein receptors on extracellular vesicles
|Nature Biomedical Engineering|2021|102
Dp71 contribution to the molecular scaffold anchoring aquaporine‐4 channels in brain macroglial cells
|Glia|2020|50
Increased creative thinking in narcolepsy
|Brain|2019|47