Targeting GLB1 in mice by CRISPR/Cas9 genome editing: Establishing a novel model for type II GM1 gangliosidosis

Elena‐Raluca Nicoli(National Institutes of Health), Cynthia J. Tifft(Children's National), Michal Tyrlík(National Institutes of Health), Yvonne L. Latour(National Institute of Neurological Disorders and Stroke), Jeeva Munasinghe Jeeva(National Institutes of Health), Danielle Donahue(National Institutes of Health), Richard L. Proia(National Institute of Diabetes and Digestive and Kidney Diseases), Robin Yoon(National Institutes of Health), Rohini Sidhu(Washington University in St. Louis), Mylene Huebecker(University of Oxford), Danielle Springer, Frances M. Platt(University of Oxford), Morteza Peiravi(National Institutes of Health), Andrea D'Souza(National Institutes of Health), Pamela Kell(Washington University in St. Louis), Maria T. Acosta, Xuntian Jiang(Washington University in St. Louis), Brianna Glase(National Institutes of Health)
Molecular Genetics and Metabolism
January 30, 2020
Cited by 0


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