AVR-RD-01 lentiviral gene therapy reduces Gb3 substrate in endothelial cells of renal peritubular capillaries in a previously untreated classic Fabry disease male patient
Birgitte Volck(ProterixBio (United States)), Chris Mason(Oak Ridge National Laboratory), Dawn Phillips(ProterixBio (United States)), B. Carnley(Royal Perth Hospital), Mark Thomas(Royal Perth Hospital), Azadeh Golipour(ProterixBio (United States)), Shari Fallet(ProterixBio (United States))
Cited by 2
Related Papers
A Brief Definition of Regenerative Medicine
|Regenerative Medicine|2007|795
BTRFS
|ACM Transactions on Storage|2013|381
Lancet Commission: Stem cells and regenerative medicine
|The Lancet|2017|276
Cell Therapy Industry: Billion Dollar Global Business with Unlimited Potential
|Regenerative Medicine|2011|144
Peak Serum: Implications of Serum Supply for Cell Therapy Manufacturing
|Regenerative Medicine|2011|144