The challenges of living with and managing epidermolysis bullosa: insights from patients and caregivers

Anna L. Bruckner(Children's Hospital Colorado), Dédée F. Murrell(Sutherland Hospital), Jayson Wisk(Amicus Therapeutics (United States)), Hjalmar Lagast(Amicus Therapeutics (United States)), Nita Patel(Amicus Therapeutics (United States)), Jayne Gershkowitz(Amicus Therapeutics (United States)), Michael Hund, Brett Kopelan(Dystrophic Epidermolysis Bullosa Research Association of America), Michael Losow(Amicus Therapeutics (United States)), A. Reha(Amicus Therapeutics (United States)), Jamie Gault(Amicus Therapeutics (United States))
Orphanet Journal of Rare Diseases
January 3, 2020
Cited by 185


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