High-Efficiency, Selection-free Gene Repair in Airway Stem Cells from Cystic Fibrosis Patients Rescues CFTR Function in Differentiated Epithelia

Sriram Vaidyanathan(Stanford University), Ameen A. Salahudeen(Stanford University), Zachary M. Sellers(Stanford University), Dawn T. Bravo(Stanford Medicine), S. S. Choi(Stanford University), Arpit Batish(Stanford University), Wei Le(Stanford Medicine), Ron Baik(Stanford University), Sean de la O(Stanford University), Milan P. Kaushik(Stanford University), Noah Galper(Stanford University), Ciaran M. Lee(Rice University), Christopher A. Teran(Stanford Medicine), Jessica H. Yoo(Stanford University), Gang Bao(Rice University), Eugene H. Chang(University of Arizona), Zara M. Patel(Stanford Medicine), Peter H. Hwang(Stanford Medicine), Jeffrey J. Wine(Stanford University), Carlos Milla(Stanford University), Tushar Desai(Stanford Medicine), Jayakar V. Nayak(Stanford Medicine), Calvin J. Kuo(Stanford Medicine), Matthew H. Porteus(Stanford University)
Cell stem cell
December 12, 2019
Cited by 132Open Access
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