Titin splicing regulates cardiotoxicity associated with calpain 3 gene therapy for limb-girdle muscular dystrophy type 2A

William Lostal(Inserm), Isabelle Richard(Inserm), Henk Granzier(University of Arizona), Jochen Gohlke(University of Arizona), Laurence Suel(Inserm), Zaher Elbeck(Uppsala University), Xidan Li(Integrated Cardio Metabolic Centre), John E. Smith(University of Arizona), Guillaume Corre(Inserm), Jack‐Yves Deschamps(Oniris), Ralph Knöll(Integrated Cardio Metabolic Centre), Heather Best(The University of Sydney), Karine Charton(Inserm), Nathalie Bourg(Inserm), Carinne Roudaut(Inserm), Marine Faivre(Inserm)
Science Translational Medicine
November 27, 2019
Cited by 26


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