Efficacy and safety of the elexacaftor plus tezacaftor plus ivacaftor combination regimen in people with cystic fibrosis homozygous for the F508del mutation: a double-blind, randomised, phase 3 trial
Harry Heijerman(University Medical Center Utrecht), Edward F. McKone(University College Dublin), D.G. Downey(Queen's University Belfast), Eva Van Braeckel(Ghent University Hospital), Steven M. Rowe(University of Alabama at Birmingham), Elizabeth Tullis(St. Michael's Hospital), Marcus Mall(German Center for Lung Research), John Welter(New York Medical College), Bonnie W. Ramsey(Seattle Children's Hospital), Charlotte McKee(Vertex Pharmaceuticals (United States)), Gautham Marigowda(Vertex Pharmaceuticals (United States)), Samuel M. Moskowitz(Vertex Pharmaceuticals (United States)), David Waltz(Vertex Pharmaceuticals (United States)), Patrick R. Sosnay(Vertex Pharmaceuticals (United States)), C Simard(Vertex Pharmaceuticals (United States)), Neil Ahluwalia(Vertex Pharmaceuticals (United States)), Fengjuan Xuan(Vertex Pharmaceuticals (United States)), Yaohua Zhang(Vertex Pharmaceuticals (United States)), Jennifer L. Taylor‐Cousar(National Jewish Health), Karen McCoy(Nationwide Children's Hospital), Karen McCoy(Nationwide Children's Hospital), Scott H. Donaldson, Seth Walker, James F. Chmiel, Ronald C. Rubenstein, Deborah Froh, Isabel P. Neuringer, Manu Jain, Kathryn Moffett, Jennifer L. Taylor‐Cousar(National Jewish Health), Bruce Barnett, Gary A. Mueller, Patrick A. Flume(Vertex Pharmaceuticals (United States)), F. R. Livingston, Nighat Mehdi, Charlotte C. Tenebäck(Vertex Pharmaceuticals (United States)), John Welter(New York Medical College), Raksha Jain, Dana G. Kissner, K. Patel, Francisco J. Calimano, Jimmy Johannes, Cori Daines, Thomas G. Keens, Herschel Scher, Subramanyam Chittivelu, Sudhakar Reddivalam, Ross C. Klingsberg, Larry G. Johnson, Stijn Verhulst, Patricia Macedo, D.G. Downey(Queen's University Belfast), Gary Connett, E.F. Nash(University College Dublin), Nicholas Withers, Timothy Lee, Marleen Bakker, Harry Heijerman(University Medical Center Utrecht), F. Vermeulen, Eva Van Braeckel(Ghent University Hospital), Christiane Knoop, Elke De Wachter, Renske van der Meer, Petrus Merkus, Christof J. Majoor
Cited by 1,351Open Access
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