A new patient‐derived iPSC model for dystroglycanopathies validates a compound that increases glycosylation of α‐dystroglycan
Jihee Kim(Queen Mary University of London), Yung‐Yao Lin(Queen Mary University of London), Pentao Liu(Hong Kong Science and Technology Parks Corporation), Pierpaolo Ala(Great Ormond Street Hospital), Sandra Louzada(Wellcome Sanger Institute), Derek L. Stemple(Wellcome Sanger Institute), Amaia Paredes‐Redondo(Queen Mary University of London), David L. Selwood(Wolfson Foundation), Silvia Torelli(University College London), Francesco Catapano(University College London), Beatrice Lana(Queen Mary University of London), Christin Luft(MRC Laboratory for Molecular Cell Biology), Evangelos Konstantinidis(Uppsala University), Beiyuan Fu(Wellcome Sanger Institute), Francesco Muntoni(Great Ormond Street Hospital), AW Edith Chan(Wolfson Foundation), David Ryan(University College Cork), Fengtang Yang(Shandong University of Technology), Elizabeth Stevens(Great Ormond Street Hospital), Robin Ketteler(MRC Laboratory for Molecular Cell Biology)
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